GeneticsAutophagyPeer-reviewed
Metformin rescues muscle function in BAG3 myofibrillar myopathy models
Avnika Ashok Ruparelia, Emily A. McKaige, Caitlin Williams…·Robert J. Bryson‐Richardson
This study identifies Metformin as a potential therapy for BAG3 myofibrillar myopathy by rescuing muscle function in zebrafish models and reducing protein aggregates in human cells.