Pharmacology & ToxicologyMolecular TherapyPeer-reviewed
AAV NRF2 Gene Therapy Preserves Retinal Structure and Function in Rodent Models of Oxidative Damage
Apolonia Gardner, Shuai Wang, Adam Daniels…·Constance L. Cepko
This paper tests AAV8/Best1-Nrf2 gene therapy in rodent models of oxidative stress, showing protection of retinal cells and preservation of visual function.