Comparison of CRISPR/Cas endonucleases for in vivo retinal gene editing.
F. Li, K. Wing, J.-H. Wang, C. D. Luu, J. A. Bender, J. Chen, Q. Wang, Q. Lu, M. T. N. T. Tran, K. M. Young, R. C. Wong, A. Pebay, A. L. Cook, S. S. Hung, G.-S. Liu, A. W. Hewitt
This study compares CRISPR/Cas endonucleases for in vivo retinal gene editing and finds SpCas9 delivered via AAV7m8 achieves the highest knockout efficacy.
bioRxiv · Jun 9, 2020Bioengineering