BioengineeringbioRxiv
Comparison of CRISPR/Cas endonucleases for in vivo retinal gene editing.
F. Li, K. Wing, J.-H. Wang…·A. W. Hewitt
This study compares CRISPR/Cas endonucleases for in vivo retinal gene editing and finds SpCas9 delivered via AAV7m8 achieves the highest knockout efficacy.
DOI 10.3389/fncel.2020.570917