NeurosciencebioRxivPreprint
Preclinical Development of a Vectorized Artificial miRNA Gene Therapy for Tauopathies
Irvin T. Garza, Brina Snyder, Sydni K. Holmes…·Rachel M. Bailey
This paper develops a gene therapy using artificial miRNA delivered via adeno-associated virus to reduce tau in a mouse model of tauopathy, showing efficacy even at late disease stages.
2 citations