BiochemistrybioRxivPreprint
Autophagy modulation enhances enzyme replacement therapy response in Fabry disease
L. Abily-Donval, F. Barbey, S. Torre…·S. Bekri
This study shows that autophagy inhibition improves enzyme replacement therapy effectiveness in Fabry disease by enhancing exogenous enzyme trafficking to lysosomes.
DOI 10.1101/2021.04.26.441451