Cell BiologybioRxiv
A novel iPSC model reveals selective vulnerability of neurons in Multiple Sulfatase Deficiency
V. Pham, L. S. Finoti, M. M. Cassidy…·R. C. Ahrens-Nicklas
This paper creates an iPSC model of Multiple Sulfatase Deficiency, showing that neurons become more vulnerable to SUMF1 loss during differentiation.
DOI 10.1016/j.ymgme.2023.108116