NeurosciencebioRxivPreprint
Allele-selective knockdown of mutant DNAJB6 improves molecular features in a primary mouse myotube model of LGMDD1
Aliasgar Vohra, Meade Haller, May M Paing…·Andrew R Findlay
This study uses allele-selective knockdown to reduce mutant DNAJB6 in a mouse model of LGMDD1, improving molecular features associated with the disease.
DOI 10.64898/2026.11.06.764697