NeurosciencebioRxivPreprint
DNAJB6 Isoform Specific Knockdown: Therapeutic Potential for LGMDD1
Andrew R. Findlay, May M. Paing, Jil Daw…·Conrad Chris Weihl
This study investigates DNAJB6 isoform-specific knockdown as a potential therapy for LGMDD1, showing that reducing DNAJB6b levels in a mouse model corrected proteomic disease signatures.
DOI 10.1101/2022.11.17.516920