NeuroscienceDisease Models & MechanismsPeer-reviewed
Four new Duchenne muscular dystrophy mouse models with clinically relevant exon deletions in the human DMD gene
Maaike van Putten, Margot M. L. Linssen, C. Tanganyika-de Winter…·Peter Hohenstein
The paper develops four humanized DMD mouse models with specific human exon deletions to test exon skipping therapies for Duchenne muscular dystrophy.
DOI 10.1242/dmm.052875