NeuroscienceActa Neuropathologica CommunicationsPeer-reviewed
Intrathecal (G4C2)149 delivery in C9orf72-deficient mice yields mild motor dysfunction and ALS/FTD pathological hallmarks
Katelyn A. Russell, Amelia A Shahrabi, Suleyman C. Akerman…·Aaron R. Haeusler
This paper delivers (G4C2)149 repeats intrathecally in C9orf72-deficient mice, revealing mild motor dysfunction and ALS/FTD pathological features.
DOI 10.1186/s40478-026-02341-8