NeurosciencebioRxivPreprint
Early AAV9-mediated SLC9A6 gene replacement preserves cerebellar structure and motor function in the shaker rat model of Christianson syndrome
Kajal Dahiya, Kaanchana Sekaran, Lingye Hu…·Collin J Anderson
This study evaluates AAV9-mediated SLC9A6 gene replacement in shaker rats, showing early treatment preserves cerebellar structure and motor function, while later treatment has diminishing effects.