NeurosciencebioRxivPreprint
Frataxin deficiency in the astrocytes drives neurocognitive impairment in sickle cell disease mice
Enrico Maria Novelli, Shane C Lenhart, Lesley M. Foley…·Rimi Hazra
This study shows that frataxin deficiency in astrocytes worsens cognitive impairment in sickle cell disease mice, suggesting FXN as a potential therapeutic target.
DOI 10.1101/2024.12.20.629760