NeurosciencebioRxivPreprint
Recombinant NAGLU-IGF2 prevents physical and neurological disease and improves survival in Sanfilippo B syndrome
Steven Q. Le, Shih‐hsin Kan, Marie S. Roberts…·Patricia Dickson
This study shows that rhNAGLU-IGF2 treatment improves disease markers, behavior, and survival in Sanfilippo B mice and dogs.