PhysiologybioRxivPreprint
Gene Therapy for Cardiomyopathy associated with Duchenne Muscular Dystrophy in a Pig Model
Andrea Bähr, Petra Hoppmann, Tarik M. Bozoglu…·Christian Kupatt
This study shows that AAV1.SERCA2a gene therapy improves heart function and reduces arrhythmia in a pig model of Duchenne muscular dystrophy.