Molecular BiologybioRxivPreprint
Probing the sub-cellular mechanisms of LCA5-Leber Congenital Amaurosis and associated gene therapy with expansion microscopy
Siebren Faber, Olivier Mercey, Katrin Junger…·Ronald Roepman
This study uses expansion microscopy to investigate LCA5-related photoreceptor defects and evaluates gene therapy efficacy in a mouse model.
DOI 10.1101/2023.01.17.524360