NeuroscienceProceedings of the National Academy of SciencesPeer-reviewed
MTSS1/Src family kinase Dysregulation Underlies Multiple Inherited Ataxias
Alexander S. Brown, Pratap Meera, Banu Altindag…·Anthony E. Oro
This study identifies MTSS1/Src family kinase dysregulation as a common mechanism in multiple inherited ataxias and shows SFK inhibitors can delay disease progression in mouse models.
30 citations