BioengineeringbioRxivPreprint
Disease exacerbation by fibroblast inclusion in Duchenne Muscular Dystrophy MYOrganoids reveals limitations of microdystrophin therapeutic efficacy
L. Palmieri, L. Pili, A. Jaber…·S. Albini
This paper develops a human DMD model using MYOrganoids to study fibroblast inclusion effects and evaluates microdystrophin therapy efficacy, finding limited success in reducing fibrosis and improving membrane stability.
DOI 10.1101/2023.07.26.550063