Transient growth factor expression via mRNA in lipid nanoparticles promotes hepatocyte cell therapy to treat murine liver diseases
A. R. Smith, F. Rizvi, E. Everton, A. Adeagbo, S. Wu, Y. Tam, H. Muramatsu, N. Pardi, D. Weissman, V. Gouon-Evans
The paper demonstrates that transient mRNA-based growth factor expression in lipid nanoparticles enhances PHH engraftment and liver function in murine liver disease models.
bioRxiv · Jan 11, 2024 · PreprintCell Biology