A temperature-sensitive and interferon-silent Sendai virus vector for CRISPR-Cas9 delivery and gene editing in primary human cells
C. S. Stevens, J. Carmichael, R. Watkinson, S. S. Kowdle, R. A. Reis, K. Hamane, J. Jang, A. Park, O. Pernet, W. Khamaikawin, P. Hong, P. A. Thibault, A. Gowlikar, D. S. An, B. Lee
This paper develops a temperature-sensitive and interferon-silent Sendai virus vector for CRISPR-Cas9 delivery, achieving high gene editing efficiency in human cells without triggering immune responses.
bioRxiv · May 3, 2024 · PreprintMicrobiology