BioengineeringbioRxivPreprint
All-in-one AAV-delivered epigenome-editing platform: proof-of-concept and therapeutic implications for neurodegenerative disorders
B. Kantor, B. Odonovan, J. Rittiner…·O. Chiba-Falek
This paper develops a compact AAV-delivered dCas9-based repressor system for gene silencing, demonstrating its effectiveness in reducing ApoE expression in vitro and in vivo.
DOI 10.1101/2023.04.14.536951