BioengineeringbioRxiv
mRNA trans-splicing dual AAV vectors for (epi)genome editing and gene therapy
L. M. Riedmayr, K. S. Hinrichsmeyer, S. B. Thalhammer…·E. Becirovic
This paper introduces REVeRT, a dual AAV vector system using mRNA trans-splicing for efficient gene delivery and editing, showing improved reconstitution and therapeutic potential in a mouse model.
DOI 10.1038/s41467-023-42386-0