BioengineeringbioRxivPreprint
Encapsulation of AAVs into protein vault nanoparticles as a novel solution to gene therapy's neutralizing antibody problem
L. T. Collins, W. Beatty, B. Moyo…·D. Curiel
This study encapsulates AAVs into protein vault nanoparticles to bypass neutralizing antibodies, enabling effective gene therapy despite preexisting immunity.
DOI 10.1101/2023.11.29.569229