Cell BiologybioRxivPreprint
Multi-Species Phenotypic Screening across Disease Models of Mucolipidosis Type IV
A. Hadjikyriacou, S. Iyer, J. D. Mast…·S. M. Canham
The paper screens a compound library across invertebrate and human models of mucolipidosis IV to identify conserved disease modifiers, finding cyclin-dependent kinase inhibition as a potential therapeutic strategy.
DOI 10.1101/2021.03.05.434120