Cancer BiologybioRxivPreprint
Prolonged XPO1 inhibition is essential for optimal anti-leukemic activity in NPM1-mutated AML
G. Pianigiani, A. Gagliardi, F. Mezzasoma…·L. Brunetti
This study shows that prolonged XPO1 inhibition is more effective than intermittent dosing in NPM1-mutated AML by achieving stable HOX downregulation and anti-leukemic activity.
DOI 10.1101/2021.12.11.472216