BioengineeringbioRxivPreprint
Preventing large deletions and chromosome loss in engineered human primary T cells by CasPlus with optimized guide RNAs
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NYU Langone HealthORCID 0000-0002-6236-7444Unclaimed ORCID profile · follow to get notified of new preprints
2 papers
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Colin T. Konishi, Nancy Mulaiese, Tanvi Butola…·Chengzu Long
This study corrects a pathogenic SERPINI1 mutation in iPSC-derived neurons using a personalized base editor to treat FENIB and related neurodegenerative diseases.