Author
Fraunhofer Institute for Translational Medicine and PharmacologyORCID 0000-0002-7415-4905Unclaimed ORCID profile · follow to get notified of new preprints
Mutual co-authors in cluster
4 papers
Recent·Most cited
Dinh-Long Huynh, Elin Asp, Flavio Ballante…·Ola Spjuth
A human-supervised multi-agent LLM system covered drug repurposing from knowledge graph building to assay analysis in three case studies; retrospective COVID-19 screen AUC-ROC 0.986 without predefined thresholds.
Lucas Tricoli, Sunetra Sase, Julia Liao Hacker…·Stefano Rivella
This paper develops a novel lentiviral vector for gene therapy of MLD that achieves high ARSA activity with minimal genomic integrations, improving safety and efficacy in preclinical models.
Vi Pham, Lucas Tricoli, Xinying Hong…·Rebecca C. Ahrens‐Nicklas
This study shows that SUMF1 gene therapy via hematopoietic stem cell transplant improves biochemical and functional outcomes in a mouse model of Multiple Sulfatase Deficiency.
Vi Pham, Lívia Sertori Finoti, Margaret M. Cassidy…·Rebecca C. Ahrens‐Nicklas
This paper creates an iPSC model of Multiple Sulfatase Deficiency, showing that neurons become more vulnerable to SUMF1 loss during differentiation.