Enveloped viruses pseudotyped with mammalian myogenic cell fusogens target skeletal muscle for gene delivery
S. Hindi, M. Petrany, E. Greenfeld, L. Focke, A. Cramer, M. Whitt, V. Prasad, J. Chamberlain, B. Podbilewicz, D. Millay
This study shows that pseudotyping enveloped viruses with muscle fusogens enables targeted gene delivery to skeletal muscle in a mouse model of Duchenne muscular dystrophy.
bioRxiv · Mar 17, 2023Cell Biology