BioengineeringbioRxiv
Focused ultrasound-mediated brain genome editing
Y.-H. Lao, R. Ji, J. K. Zhou…·K. W. Leong
This paper demonstrates a method to edit the brain genome in mammals using focused ultrasound to temporarily open the blood-brain barrier for CRISPR/Cas9 delivery via intravenous injection.
DOI 10.1073/pnas.2302910120