BioengineeringbioRxivPreprint
Targeted genome editing restores auditory function in adult mice with progressive hearing loss caused by a human microRNA mutation
W. Zhu, W. Du, A. P. Rameshbabu…·Z.-Y. Chen
This study uses genome editing in adult mice with a MIR96 mutation to restore hearing, showing efficacy that improves with earlier intervention.
DOI 10.1101/2023.10.26.564008