BioengineeringbioRxiv
Engineering self-deliverable ribonucleoproteins for genome editing in the brain
K. Chen, E. C. Stahl, M. H. Kang…·J. A. Doudna
This study engineers self-deliverable CRISPR ribonucleoproteins for efficient genome editing in neural progenitor cells and mouse brain tissue.
DOI 10.1038/s41467-024-45998-2