Gene Therapy for Cardiomyopathy associated with Duchenne Muscular Dystrophy in a Pig Model
A. Baehr, P. Hoppmann, T. Bozoglu, M. Stirm, I. Luksch, T. Ziegler, N. Hornaschewitz, S. Shresta, B. Shashikadze, J. B. Stöckl, N. Raad, H. Blum, S. Krebs, T. Fröhlich, C. Baumgartner, , C. Kupatt
This study shows that AAV1.SERCA2a gene therapy improves heart function and reduces arrhythmia in a pig model of Duchenne muscular dystrophy.
bioRxiv · Oct 2, 2023 · PreprintPhysiology